Current Projects and Funding Opportunities
The function of ganglioside in brain health
The function of ganglioside in brain health
Explore ongoing projects to understand how gangliosides lead to neurodegeneration in GM3 synthase deficiency and other neurological diseases
Therapeutics for GM3SD
The function of ganglioside in brain health
Explore gene therapy and other innovative treatments
Natural History
Explore natural history projects to understand the clinical manifestations of this disease
Current Clinical Trials
Coming soon
Developing Animal Models
Understanding genomic and phenotypic variability
Coming Soon
Understanding genomic and phenotypic variability
Understanding genomic and phenotypic variability
Understanding the differences in how GM3 synthase deficiency presents